Browsing: Rare Disease
As government-supported research in the US is being decimated by funding cuts, it was refreshing to attend REMEDi4ALL’s international drug…
Right now, Congress has a chance to save the lives of countless sick children—without spending a dime of taxpayer money.…
Innovative approaches to drug discovery are needed to help find effective treatments for the myriad of diseases that afflict humanity.…
Rocket Pharmaceuticals celebrated its sixth annual Rare Disease Day event bringing together leaders in the biotech community along with patients,…
Matt Goldstein and his wife, Myra Sack, lost their first child, Havi, to the fatal genetic disease, Tay Sachs, in…
Serendipity, persistence, and rigor have played a role in the foundation and discovery processes of some of the most innovative…